A long-established drug with a diverse medical history is drawing new attention for its potential role in treating an ultra-rare and life-threatening genetic disorder. Early findings suggest that a medicine first developed decades ago could take on an unexpected new role in treating Bachmann-Bupp syndrome (BABS), a devastating and ultra-rare condition with no established therapy. […]
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Home Blog Decades-Old Drug May Offer First Real Hope for Ultra-Rare, Life-Threatening Genetic Disorder